Abstract

SMA Newborn Screening Test and Gene Replacement Therapy in Chiba Prefecture"

Speaker: Dr. Hiromi Aoyama, Medical Director, Department of Neurology, Chiba Children's Hospital

"A sister case of spinal muscular atrophy treated with Zolgensma"

Speaker: Dr. Takahito Inoue, Director of Pediatrics, Chikushi Hospital, Fukuoka University

"Knowledge and ingenuity from 6 cases of zolgensuma administration including NBS" 

Speaker: Dr. Yusaku Miyamoto, Professor, Department of Pediatrics, St. Marianna University School of Medicine

Closing：The Importance and Challenges of Publicly Funded NBS and the Establishment of a Medical Care System

Presenter: Tochigi Prefectural Rehabilitation Center Director / Medical Director Dr. Takamichi Yamagata

Speakers